Company Name: Ultragenyx Pharmaceutical Inc.
Ultragenyx Pharmaceutical Inc. is a clinical-stage biopharmaceutical company. The company is engaged in the development of therapies designed to treat rare/ultra-rare diseases. The company’s focus is on serious genetic diseases. The company’s pipeline includes product candidates designed to treat a variety of conditions including:
- Galactosialidosis
- Glucose Transporter 1 Deficiency (Glut1 DS)
- GNE Myopathy (GNEM)
- Long-Chain Fatty Acid Oxidation Disorders (FAOD)
- Mucopolysaccharidosis 7 (MPS 7)
- Tumor-Induced Osteomalacia (TIO)
- X-Linked Hypophosphatemia (XLH)
Ticker Symbol: RARE (NASDAQ)
Company Website: www.ultragenyx.com
Social Media: Ultragenyx Pharmaceutical LinkedIn Page
Classification: Biotech
Areas of Focus: Rare Diseases
Headquarters: Novato, California
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