Company Name: Bio Blast Pharma Ltd.
Bio Blast Pharma Ltd. is a clinical-stage biotechnology company. The company is engaged in the development of therapies designed to treat rare and ultra-rare genetic diseases. The company’s pipeline includes product candidates for a variety of rare diseases including:
- Oculopharyngeal Muscular Dystrophy
- Spinocerebellar Ataxia Type 3
- Spinal Muscular Atrophy
- Friedreich’s Ataxia
- Ornithine Transcarbamylase Deficiency
Ticker Symbol: ORPN (NASDAQ)
Company Website: http://bioblast-pharma.com
Company Profile: Bio Blast Pharma LinkedIn Page
Headquarters: Tel Aviv, Israel