Company Name: Bio Blast Pharma Ltd.

Bio Blast Pharma Ltd. is a clinical-stage biotechnology company. The company is engaged in the development of therapies designed to treat rare and ultra-rare genetic diseases. The company’s pipeline includes product candidates for a variety of rare diseases including:

  • Oculopharyngeal Muscular Dystrophy
  • Spinocerebellar Ataxia Type 3
  • Spinal Muscular Atrophy
  • Friedreich’s Ataxia
  • Ornithine Transcarbamylase Deficiency

Ticker Symbol: ORPN (NASDAQ)

Company Website:

Company Profile: Bio Blast Pharma LinkedIn Page

Headquarters: Tel Aviv, Israel